About
Started by one family in Helsinki. Built for every child with this gene.
Who we are
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Who we are. Placeholder — we will write this in our own words.
Why we are doing this. Placeholder — we will write this in our own words.
Our strategy
Repurposing first: the fastest route to something that could help children soon
Tools and data: models, biomarkers, a registry of families
Gene therapy, kept ready for when the field is
Every euro buys a named result with a date.
Support the researchBoard
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Scientific advisors
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How we handle money
Written deliverables before any payment.
Open results.
Quarterly reports to donors.
100% to research, the family carries every other cost.